The Lancet Child & Adolescent Health
ISSN: 2352-4642
eISSN: 2352-4650
Publisher: Elsevier
Publications (2)
Gene replacement therapy with onasemnogene abeparvovec in children with spinal muscular atrophy aged 24 months or younger and bodyweight up to 15 kg: an observational cohort study (2022)
Weiß C, Ziegler A, Becker LL, Johannsen J, Brennenstuhl H, Schreiber G, Flotats-Bastardas M, et al.
Journal article
Life-threatening infections in children in Europe (the EUCLIDS Project): a prospective cohort study. (2018)
Martinón-Torres F, Salas A, Rivero-Calle I, Cebey-López M, Pardo-Seco J, Boeddha NP, Klobassa DS, et al.
Journal article